The ALS Association and the Packard Center Partner to Develop Animal Model Systems for Most Common Cause of Familial ALS

“Following the discovery of the most abundant genetic cause of ALS, we have initiated a drug development approach to selectively destroy the ALS-causing product of the mutated gene…”

Categories: Research News  |  Tags: ALS, ALS Association, ALSA, antisense oligonucleotide, ASO, biomarkers, Bryan J. Traynor M.D., C9orf 72 gene, C9ORF72 gene, C9ORF72 mRNA, Don W. Cleveland, hexanucleotide, hexanucleotide GGGGCC, Jeff Rothstein, Johns Hopkins University, Laboratory of Neurogenetics National Institute on Aging, Lou Gehrig's disease, Lucie Bruijn Ph.D, Molecular Medicine University of California San Diego, neurodegeneration, Ph.D, Philip C. Wong Ph.D., Piera Pasinelli Ph.D., RASCALS Foundation, Robert A. Stehlin Campaign for ALS, Robert Packard Center, Robert Packard Center for ALS Research at Johns Hopkins, St.Louis RASCALS ALS Lou Gehrig's Disease amotrophic lateral sclerosis  |  No comments